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- PP405 mitochondrial pyruvate carrier (MPC) inhibitor by Pelage in early trials
- Valproic acid Anti-seizure and mood-stabilising drug
- Tofacitinib JAK inhibitor pill, an immune-system drug
- Minoxidil Vasodilator used on the scalp and, at low doses, as a tablet
- Bicalutamide Nonsteroidal anti-androgen, originally a prostate cancer drug