The treatment was not recommended due to limited effectiveness and significant side effects.
11 citations
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January 2009 in “World Journal of Gastroenterology” A woman with both Cronkhite-Canada syndrome and myelodysplastic syndrome improved significantly with corticosteroid treatment.
January 2025 in “HemaSphere” The term "low-risk" in myelodysplastic syndrome is misleading and should be changed to better reflect patient experiences and needs.
30 citations
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January 2007 Cyclophosphamide can cause serious short-term and long-term side effects, including increased cancer risk and infertility.
1 citations
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October 2022 in “Molecular therapy” The FDA approved the first gene therapy for a blood disorder after overcoming early challenges and demonstrating patient benefits.